The PPMD Town Hall on Clinical Trials is underway TODAY, March 4th, during PPMD's 2024 Advocacy Conference in Washington, D.C.!
This meeting is a platform for families impacted by Duchenne and Becker to share their experiences and insights on past, present, and future clinical trials. The primary goal is to hear directly from families and gather valuable input to shape PPMD's advocacy efforts, especially in interactions with the FDA on drug development.
AGENDA HIGHLIGHTS:
- Parent/Patient Panel: Diverse voices at different ages and stages sharing their clinical trial experiences, discussing challenges, and expressing hopes for outcomes.
- Professional Panel on Patient Preference and Clinical Trials: Featuring a representative from FDA CDER and clinicians covering FDA updates, issues in clinical trials, and potential solutions.
Following the meeting, a recap will be shared with the community and learnings will be integrated into PPMD's advocacy strategy moving forward as we interact with federal agencies (including FDA, NIH, DOD, and CDC). Together, we're working to enhance the clinical trial landscape for Duchenne and Becker families and contribute to policy strategies for improved outcomes. #PPMDAdvocacy
Pleasure to partner with you on this, Raviv Pryluk - #patients indeed deserve better #clinicaltrials = greater hope. 🙏