Vitaccess’ Post

Real-world evidence (RWE) is currently a buzzword in the pharmaceutical industry. Here is an overview of RWE's value throughout the entire product life cycle from Tsitsi Monera-Penduka, PhD ##rwe #realworldevidence #realworlddata

This great read outlines the role of RWE in clinical development. For geneticists operating in the age of growing multi-omics repositories, RWE presents a platform to fine-tune genotype-phenotype matching. Thanks Tsitsi Monera-Penduka, PhD!

#ICYMI: Nazim Kanji, Executive Director of Pediatric Services, speaks on the challenges of rare disease development in this article with Manufacturing Chemist. Read here: https://bit.ly/4950uvQ

If you are planning rare disease research, this webinar recording is a must see. Learn how early market-access evidence planning for your orphan drug can help gather the right evidence for reimbursement and access - the first time. View now. http://ow.ly/twtw50J9VHv #marketaccess #drugdevelopment

US & #APAC Rare Disease Pharma & #Biotech Leaders: Did an #FDA setback derail your #raredisease therapy development? The European pathway could be your strategic advantage. The #EMA offers: 💚 Alternative pathways: Flexibility in trial design & accelerated assessment for unmet needs. 💚 Valuable insights: Address FDA concerns using EMA feedback. 💚 Early market access: Potentially secure approval & generate data for US payers. Dive into part 2 of our "Don't Sleep on the EU" series: The Global Ambition: Mastering Dual Submission for Rare Disease Therapies. https://lnkd.in/dGSGHCuR 💛 Next week's final article, "Hurdles to Harmonization," explores how to leverage EU success for a triumphant return to the #FDA after experiencing a setback. Stay tuned! #biotech #pharma #globalstrategy #drugdevelopment #clinicaltrials #marketaccess

Join Pharmaceutical Executive and colleagues at Herspiegel this Thursday, February 15th at 11 am ET to learn about strategies and unique considerations for commercializing novel therapies to treat rare diseases. Our team of experts will provide insight into potential challenges and tactics for ensuring a successful launch. Don't miss out on this valuable opportunity to gain knowledge and stay ahead of the curve in the pharmaceutical industry. #Pharmaceuticals #RareDiseases #Commercialization #IndustryInsights

According to the European Organization for Rare Diseases (EURORDIS) there are over 300 million people living with one or more of over 6,000 identified rare diseases around the world. This is equivalent to the population of the world’s third largest country. With Rare Disease day this year falling on 29th February, the rarest day of the year, there is an opportunity to reflect on what still needs to be done to ensure equity in access to diagnostics and treatments for rare diseases. In this blog, my colleague & Deallus Rare Disease expert Hormoz M. reflects on the great advances we have seen over the past 20 years in driving new treatment options within rare diseases. #rarediseaseday #rarediseaseawareness #healthequity

On this #RareDiseaseDay, we are raising awareness of the remarkable strength and resilience of individuals and families affected by rare diseases around the world. With STADA's Specialty Pharma segment, we deliver medicines to improve the lives and clinical outcomes of patients worldwide with chronic, complex or rare diseases. #CaringForPeoplesHealth #RareDiseaseDay #RareDiseaseDay2024

The global #IBD treatment market is expected to further expand in coming years driven by the launch of follow-on refined biologics, with the prospect of longer-term specially engineered 'Tregs' (cellular interventions) that act to dampen the host auto-immune response in affected patients...

There's still time to register for this expert webinar! » https://bit.ly/3wEFJta The world of drug development is evolving with the increased acceptance of real-world evidence (RWE). Disease registries, one of the most clinically rich sources of real-world data (RWD), are at the forefront of this change. These registries are purpose-built for research, allowing the collection of fit-for-purpose data, especially in rare diseases. Register for this expert webinar to gain insights into how RWE and RWD from registries enhance clinical development, approval and post-marketing analyses, particularly for rare diseases.